Eric J. Sorenson, M.D.

Open

• An Open-label Single Center, Single Participant Study Of An Experimental Antisense Oligonucleotide Treatment For Amyotrophic Lateral Sclerosis (ALS) Due To CHCHD10 Gene Mutation Rochester, MN This research project entails delivery of a personalized antisense oligonucleotide (ASO) drug designed for a single participant with amyotrophic lateral sclerosis (ALS) due to a pathogenic variant in CHCHD10
• PLS Natural History Study (PLS) Jacksonville, FL Rochester, MN

  The purpose of this study is to develop a natural history dataset and biorepository of early Primary Lateral Sclerosis (PLS) and well-established PLS cases for future clinical trials.